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Attending at the I st International Conference on dwarfism
This last saturday was a day to know more and go beyond myself/ourselves. The conference was in Lisbon and it lasted one day long. I was quite glad when I found about the conference, through our...
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Orphan drugs summit 2014 – Copenhagen, 17th – 19th September
This September, it will be discussed crucial topics around orphan drugs. Far beyond the scientific studies, laboratory development of the drugs, the clinical trials, all the permissions needed from...
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Achondroplasia: A Model for Clinic-based Research
This is a quite interesting lecture by Prof. Richard Pauli, released by University of Winsconsin School of Medicine and Public Health. It´s a pleasent session, easy to hear and simplifies some medical...
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The ECRAN/ECRIN meeting
The ECRAN/ECRIN meeting was very enlightening. I meet new people, from all over Europe, USA and Canada and heard their experience, knowledge and concerns about clinical trials. The presentations were...
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BioMarin at the Wells Fargo 9th Annual Healthcare Conference
Dan Oppenheimer, Group Vice President, Development & Portfolio Strategy – BioMarin Pharmaceutical Inc, presented today at the Wells Fargo research conferences the actual state of art of BioMarin´s...
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Orphan Drugs Summit 2014 – Media partner
We are just two days of this great event and I’m honored to have been chosen to participate as a media partner. The Orphan Drugs Summit is the leading rare disease event in Northern Europe. A...
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Achondroplasia highlights
During three full days, the V International Congress around Achondroplasia and other Skeletal Dysplasia took place in the north of Spain, very well-organized by Alpe Foundation. Several world-renowned...
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Soluble FGFR3 rectification
In my last post, about the V International congress around achondroplasia and other skeletal dysplasia, I mentioned the participation of Dr. Elvire Gouze and her lecture. She is responsable for the...
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BMN-111 clinical trial update
Recently, I had valid information that BioMarin announced that the measurement study is now open for recruitment again for the multicenter study. However, BioMarin didn´t change the age requirement, so...
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